Atlas Trials

GM1 Gangliosidosis

13 clinical trials · Condition

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RecordFirmDate
GM1 and GM2 Gangliosidosis PROspective Neurological Disease TrajectOry Study (PRONTO) (NCT05109793)Azafaros B.V.2022-02-22
ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening Program (NCT05368038)Albert Einstein College of Medicine2021-05-10
Study of Safety, Tolerability and Efficacy of PBGM01 in Pediatric Participants With GM1 Gangliosidosis (NCT04713475)Gemma Biotherapeutics2021-03-17
Natural History Study of Infantile and Juvenile GM1 Gangliosidosis (GM1) Patients (NCT04041102)University of Pennsylvania2020-06-12
Registry Gangliosidoses (NCT04624789)SphinCS Lyso Gemeinnutzige UG (Haftungsbeschrankt)2020-06-08
Interviews and Video Capture in Patients With GM1 Gangliosidosis (NCT04310163)LYSOGENE2020-04-20
Natural History Study for Pediatric Patients With Early Onset of Either GM1 Gangliosidosis, GM2 Gangliosidoses, or Gaucher Disease Type 2 (NCT04470713)Idorsia Pharmaceuticals Ltd.2019-07-31
HSCT for High Risk Inherited Inborn Errors (NCT00383448)Masonic Cancer Center, University of Minnesota2006-09-01
Stem Cell Transplant for Inborn Errors of Metabolism (NCT00176904)Masonic Cancer Center, University of Minnesota1995-01-01

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