Natural History Study for Pediatric Patients With Early Onset of Either GM1 Gangliosidosis, GM2 Gangliosidoses, or Gaucher Disease Type 2

Clinical trial NCT04470713 · COMPLETED

Trial details

NCT number: NCT04470713
Sponsor: Idorsia Pharmaceuticals Ltd.
Status: COMPLETED
Study type: OBSERVATIONAL

GM1 Gangliosidosis GM2 Gangliosidosis Gaucher Disease, Type 2 Tay-Sachs Disease AB Variant Gangliosidosis GM2 Sandhoff Disease

Start date: 2019-07-31
Primary completion: 2021-10-30
Enrollment: 226

View on ClinicalTrials.gov

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