Study of Safety, Tolerability and Efficacy of PBGM01 in Pediatric Participants With GM1 Gangliosidosis

Clinical trial NCT04713475 · ACTIVE_NOT_RECRUITING

Trial details

NCT number: NCT04713475
Sponsor: Gemma Biotherapeutics
Status: ACTIVE_NOT_RECRUITING
Phase: Phase 1, Phase 2
Study type: INTERVENTIONAL

GM1 Gangliosidosis GM1 Gangliosidosis, Type I GM1 Gangliosidosis, Type 2 Beta-Galactosidase-1 (GLB1) Deficiency

Start date: 2021-03-17
Primary completion: 2028-02-01
Enrollment: 26

View on ClinicalTrials.gov

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