Atlas Trials

Registry Gangliosidoses

Clinical trial NCT04624789 · UNKNOWN

Trial details

NCT number
NCT04624789
Sponsor
SphinCS Lyso Gemeinnutzige UG (Haftungsbeschrankt)
Status
UNKNOWN
Study type
OBSERVATIONAL
GangliosidosesGM1 GangliosidosisMorquio B DiseaseSialidosisGalactosialidosisGm2-Gangliosidosis, Variant B1Tay-Sachs DiseaseSandhoff DiseaseGM2 Activator Deficiency
Start date
2020-06-08
Primary completion
2020-06-12
Enrollment
40

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