| European Rare Blood Disorders Platform (ENROL) (NCT06250595) | Hospital Universitari Vall d'Hebron Research Institute | 2022-07-01 |
| Long-term Clinical Study of CN128 in Thalassemia With Sever Liver Iron Overloaded Patients (NCT05355766) | Hangzhou Zede Pharma-Tech Co., Ltd. | 2022-06-13 |
| Inhibitory Effect of a Polyphenol Supplement on Dietary Iron Absorption in Adults with Thalassemia (NCT05326503) | Swiss Federal Institute of Technology | 2022-06-01 |
| the Safety and Efficacy Evaluation of HGI-001 Injection in Patients With Transfusion-Dependent β-Thalassemia (NCT05864170) | Shenzhen Hemogen | 2022-05-27 |
| Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Transfusion-Dependent β-Thalassemia (TDT) (NCT05356195) | Vertex Pharmaceuticals Incorporated | 2022-05-03 |
| A Study of Etavopivat in Patients With Thalassemia or Sickle Cell Disease (NCT04987489) | Forma Therapeutics, Inc. | 2022-03-28 |
| Red Blood Cell - IMProving trAnsfusions for Chronically Transfused Recipients (NCT05255445) | Westat | 2022-03-16 |
| Thalassemia Knowledge in Young People of Indonesia (NCT04706585) | Fakultas Kedokteran Universitas Indonesia | 2021-06-01 |
| A Long-term Follow-up Study in Participants Who Received CTX001 (NCT04208529) | Vertex Pharmaceuticals Incorporated | 2021-01-20 |
| Safety and Efficacy Evaluation of β-globin Restored Autologous Hematopoietic Stem Cells in β-thalassemia Major Patients (NCT05745532) | Shenzhen Hemogen | 2020-12-01 |
| A Study of IMR-687 in Subjects With Beta Thalassemia (NCT04411082) | Cardurion Pharmaceuticals, Inc. | 2020-10-16 |
| Assessment of Nutritional Status and Role of Insulin-like Growth Factor-1 in Children (NCT05529550) | Menoufia University | 2020-10-01 |
| ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders (NCT04398628) | American Thrombosis and Hemostasis Network | 2020-09-30 |
| Long-term Clinical Study of CN128 in Thalassemia Patients (NCT04614779) | Hangzhou Zede Pharma-Tech Co., Ltd. | 2020-09-30 |
| The Role of OCTA in Patients Affected by Beta Thalassemia (NCT04582110) | Federico II University | 2019-10-01 |
| Hydroxyurea Therapy: Optimizing Access in Pediatric Populations Everywhere (NCT03825341) | St. Jude Children's Research Hospital | 2019-06-10 |
| Safety Study for Beta Thalassemia Subjects on PTG-300 (NCT04054921) | Protagonist Therapeutics, Inc. | 2019-05-10 |
| A Study to Determine the Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of AG-348 in Adult Participants With Non-transfusion-dependent Thalassemia (NCT03692052) | Agios Pharmaceuticals, Inc. | 2019-03-20 |
| A Blood Stem Cell Transplant for Sickle Cell Disease (NCT03249831) | City of Hope Medical Center | 2019-01-04 |
| iHSCs With the Gene Correction of HBB Intervent Subjests With β-thalassemia Mutations (NCT03728322) | Allife Medical Science and Technology Co., Ltd. | 2019-01-01 |
| Study of PTG-300 in Non-Transfusion Dependent and Transfusion-Dependent Beta-Thalassemia Subjects With Chronic Anemia (NCT03802201) | Protagonist Therapeutics, Inc. | 2018-12-19 |
| Short-term Clinical Study of CN128 in Thalassemia Patients (NCT03935633) | Hangzhou Zede Pharma-Tech Co., Ltd. | 2018-12-03 |
| A Safety and Efficacy Study Evaluating CTX001 in Participants With Transfusion-Dependent β-Thalassemia (NCT03655678) | Vertex Pharmaceuticals Incorporated | 2018-09-14 |
| Adiponectin, IL-6 and hsC-RP in Relation to Carotid Intima-media Thickness in B-thalassemia Patients (NCT03170245) | Assiut University | 2018-08-01 |
| Cerebrovascular Reserve and White Matter Disease in Patients with Chronic Anemia (NCT03715972) | Children's Hospital Los Angeles | 2018-07-15 |
| Haploidentical Allogeneic Hematopoietic Stem Cell Transplantation (HaploHCT) Following Reduced Intensity Conditioning (RIC) for Selected High Risk Non-Malignant Diseases (NCT03367546) | Masonic Cancer Center, University of Minnesota | 2018-07-02 |
| Conditioning Regimen for Allogeneic Hematopoietic Stem-Cell Transplantation (NCT03513328) | University of Florida | 2018-06-15 |
| Immunomodulatory Vitamin D in Thalassemia (NCT03919812) | Universitas Padjadjaran | 2018-04-01 |
| Colla Corii Asini Treating Anemia in Pregnant Women With Thalassemia(Presenting the Syndrome of Blood Deficiency) (NCT03374111) | The First Affiliated Hospital, Guangzhou University of Traditional Chinese Medicine | 2018-03-01 |
| A Study to Determine the Efficacy and Safety of Luspatercept in Adults With Non Transfusion Dependent Beta (β)-Thalassemia (NCT03342404) | Celgene | 2018-02-05 |
| Clinical Study of CN128 in Thalassemia Patients (NCT03673085) | Hangzhou Zede Pharma-Tech Co., Ltd. | 2018-01-05 |
| Efficacy and Safety of Low Dose Thalidomide in Transfusion Dependent Thalassemia (NCT03651102) | Blood Diseases Clinic | 2018-01-01 |
| Fludarabine Phosphate, Cyclophosphamide, Total Body Irradiation, and Donor Stem Cell Transplant in Treating Patients With Blood Cancer (NCT03333486) | Roswell Park Cancer Institute | 2017-12-07 |
| Quality of Life and Treatment Satisfaction in β-Thalassemia Patients Receiving Deferasirox (NCT03358498) | Assiut University | 2017-12-01 |
| Study on the Mechanism of Colla Corri Asini in the Treatment of Thalassemia Patients With Pregnancy Anemia (NCT03392298) | The First Affiliated Hospital, Guangzhou University of Traditional Chinese Medicine | 2017-12-01 |
| Study of Thiotepa and TEPA Drug Exposure in Pediatric Hematopoietic Stem Cell Transplant Patients (NCT03609840) | University of California, San Francisco | 2017-05-24 |
| Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of ISIS 702843 Administered Subcutaneously to Healthy Volunteers (NCT03165864) | Ionis Pharmaceuticals, Inc. | 2017-05-09 |
| The Effective and Safety of Thalidomide in TI (NCT03184844) | Xiao-Lin Yin | 2017-05-02 |
| Sofosbuvir/Ledipasvir for Hepatitis C Genotype 1-6 in Patients With Transfusion-Dependent Thalassemia: An Open Label Trial (NCT03032666) | Ala'a Sharara | 2017-05-01 |
| Hemoglobinopathy Nursing Program and Pediatric Nursing Students (NCT05389891) | Beni-Suef University | 2017-02-27 |
| Long Term Follow-up Study for Patients Enrolled on the BP-004 Clinical Study (NCT03733249) | Bellicum Pharmaceuticals | 2017-01-01 |
| The Effective and Safety of Thalidomide in NTDT (NCT02995707) | Xiao-Lin Yin | 2016-09-01 |
| L-arginine Versus Sildenafil in Children With Beta Thalassemia Associated With Pulmonary Hypertension (NCT03402191) | Sherief Abd-Elsalam | 2016-07-01 |
| Allogeneic SCT of CordIn™, in Patients With Hemoglobinopathies (NCT02504619) | Gamida Cell ltd | 2016-04-04 |
| Study of Clofarabine and Fludarabine Drug Exposure in Pediatric Bone Marrow Transplantation (HCT) (NCT03609814) | University of California, San Francisco | 2016-01-26 |
| The Prevalence and Severity of HCV Infection in Thalassemia Major and Thalassemia Intermedia in Siriraj Hospital (NCT02904252) | Mahidol University | 2016-01-01 |
| Study of Melphalan Drug Exposure in Pediatric Hematopoietic Stem Cell Transplant Patients (NCT03609827) | University of California, San Francisco | 2015-09-01 |
| CINC424A2X01B Rollover Protocol (NCT02386800) | Novartis Pharmaceuticals | 2015-03-05 |
| Therapeutic Effect of Colla Corii Asini on Improving Anemia and Hemoglobin Composition in Pregnant Women With Thalassemia (NCT02772016) | Yanfang Li | 2015-03-01 |
| Haploidentical Hematopoietic Stem Cell Transplantation (NCT02165007) | Catherine Bollard | 2015-01-01 |
| Extension Study to Evaluate the Safety and Efficacy of Luspatercept in Participants With β-Thalassemia Previously Enrolled in A536-04 (A536-06/MK-6143-004) (NCT02268409) | Acceleron Pharma, Inc., a wholly-owned subsidiary of Merck & Co., Inc., Rahway, NJ USA | 2014-10-20 |
| Use of Mobile Technology for Intensive Training in Medication Management (NCT02133560) | Duke University | 2014-05-01 |
| Nonmyeloablative Peripheral Blood Mobilized Hematopoietic Precursor Cell Transplantation for Sickle Cell Disease and Beta-thalassemia in People With Higher Risk of Transplant Failure (NCT02105766) | National Heart, Lung, and Blood Institute (NHLBI) | 2014-04-21 |
| Amlodipine for Myocardial Iron in Thalassemia (NCT02065492) | Aga Khan University | 2014-02-01 |
| A Case Control Study to Evaluate the Cognitive and Brain Function of β-thalassemia Patients. (NCT01935661) | HaEmek Medical Center, Israel | 2013-09-01 |
| Zinc Supplementation on Cellular Immunity in Thalassemia Major (NCT03117192) | Fakultas Kedokteran Universitas Indonesia | 2013-09-01 |
| Pneumococcal Vaccination for Splenectomised Thalassemia Major Patients in Indonesia (NCT03095326) | Fakultas Kedokteran Universitas Indonesia | 2013-09-01 |
| Zinc and Diabetes in Patients With Thalassemia: a Pilot Study (NCT01772680) | UCSF Benioff Children's Hospital Oakland | 2012-11-01 |
| Bone Marrow and Kidney Transplant for Patients With Chronic Kidney Disease and Blood Disorders (NCT01758042) | Massachusetts General Hospital | 2012-11-01 |
| Amlodipine in the Prevention and Treatment of Iron Overload in Patients With Thalassemia Major (NCT01395199) | University of Campinas, Brazil | 2012-08-01 |
| Multicenter Observational Study on Myocardial Iron Overload in 3 Multitransfused Populations (NCT01911871) | Assistance Publique - Hôpitaux de Paris | 2012-03-01 |
| Effects of Transfusion of Older Stored Red Cells (NCT01534676) | Columbia University | 2012-02-01 |
| Demographic, Clinical, Laboratory and Genetical Characteristics of Patients With Beta Thalassemia Intermedia (NCT01443312) | HaEmek Medical Center, Israel | 2011-10-01 |
| Renal Function Among Thalassemia Patients Treated by a Oral Chelator Deferasirox (NCT01905774) | HaEmek Medical Center, Israel | 2011-03-01 |
| Study of Fludarabine Drug Exposure in Pediatric Bone Marrow Transplantation (NCT01316549) | University of California, San Francisco | 2011-01-01 |
| Genes Influencing Iron Overload State (NCT01158794) | St. Jude Children's Research Hospital | 2010-09-21 |
| Alefacept and Allogeneic Hematopoietic Stem Cell Transplantation (NCT01319851) | Emory University | 2010-09-01 |
| Multi-Center Study of Iron Overload: Survey Study (MCSIO) (NCT01913548) | UCSF Benioff Children's Hospital Oakland | 2010-03-31 |
| Efficacy and Safety of Desferal Versus Osveral in Transfusional Iron Overload (NCT01369719) | Hormozgan University of Medical Sciences | 2010-02-01 |
| Multi-Center Study of Iron Overload: Pilot Study (NCT01114776) | UCSF Benioff Children's Hospital Oakland | 2009-11-01 |
| Assessment of Pain in People With Thalassemia Who Are Treated With Regular Blood Transfusions (NCT00872833) | Carelon Research | 2009-07-01 |
| Blood Transfusions in Thalassemia Patients, Complications and Adverse Effects (NCT00971880) | HaEmek Medical Center, Israel | 2009-05-01 |
| Sildenafil to Improve Exercise Capacity in People With Thalassemia and Pulmonary Hypertension (NCT00872170) | Carelon Research | 2009-03-01 |
| Assessment of Pain in People With Thalassemia (NCT00872339) | Carelon Research | 2009-03-01 |
| Glutamine Therapy for Hemolysis-Associated Pulmonary Hypertension (NCT01048905) | UCSF Benioff Children's Hospital Oakland | 2009-03-01 |
| Allo-HCT MUD for Non-malignant Red Blood Cell (RBC) Disorders: Sickle Cell, Thal, and DBA: Reduced Intensity Conditioning, Co-tx MSCs (NCT00957931) | Stanford University | 2009-03-01 |
| The Spleen in Sickle Cell Anemia and Sickle Cell Thalassemia (NCT00971698) | HaEmek Medical Center, Israel | 2009-02-01 |
| Iron Overload and Growth Velocity in Thalassemia and Sickle Cell Anemia (NCT00972231) | HaEmek Medical Center, Israel | 2009-01-01 |
| Reduced Intensity Conditioning for Umbilical Cord Blood Transplant in Pediatric Patients With Non-Malignant Disorders (NCT00744692) | Duke University | 2008-10-01 |
| Unrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood Cells (NCT00730314) | Children's Hospital Los Angeles | 2008-08-01 |
| Iron Balance Study of Deferasirox, Deferoxamine and the Combination of Both (NCT00738413) | Weill Medical College of Cornell University | 2008-08-01 |
| Oral Nifedipine to Treat Iron Overload (NCT00712738) | National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) | 2008-06-20 |
| Bone Marrow for Hemoglobinopathy Research (NCT00669305) | St. Jude Children's Research Hospital | 2008-05-15 |
| Sickle Cell Anemia Screening and Prevention in Northern Israel (NCT00735488) | HaEmek Medical Center, Israel | 2008-05-01 |
| Clinical Diagnosis of Teenagers Admitted to Pediatric Departments (NCT00735540) | HaEmek Medical Center, Israel | 2008-05-01 |
| Evaluating the Safety and Effectiveness of Decitabine in People With Thalassemia Intermedia (NCT00661726) | Carelon Research | 2008-01-01 |
| Phase I Study to Examine the Effect of Deferasirox on Renal Hemodynamics in β-thalassemia Patients With Transfusional Iron Overload (NCT00560820) | Novartis Pharmaceuticals | 2007-09-01 |
| Combined Chelation Therapy in Patients With Transfusion Dependent Thalassemia and Iron Overload (NCT00901199) | Elliott Vichinsky | 2007-09-01 |
| Evaluating People With Thalassemia: The Thalassemia Longitudinal Cohort (TLC) Study (NCT00661804) | Carelon Research | 2007-05-01 |
| Pegasys® Plus Ribavirin in Thalassemic Patients With Hepatitis C Virus Infection (NCT00707850) | Baqiyatallah Medical Sciences University | 2007-05-01 |
| Endocrine and Nutritional Assessment in B Thalassemia Major (NCT00456690) | HaEmek Medical Center, Israel | 2007-05-01 |
| Detection of β Thalassemia Carriers by Red Cell Parameters Obtained From the H2 Automatic Counter (NCT00481221) | HaEmek Medical Center, Israel | 2007-03-01 |
| Related Hematopoietic Stem Cell Transplantation (HSCT) for Genetic Diseases of Blood Cells (NCT02512679) | Children's Hospital Los Angeles | 2007-02-01 |
| T2* in Transfusion Dependant Anemia, MI, LVF, Normal Patients (NCT00520559) | Imperial College London | 2007-01-01 |
| The Change of Coagulation Markers in Children With β-thalassemia Disease After Stem Cell Transplantation (NCT00789516) | Mahidol University | 2006-06-01 |
| Zinc & Bone Health in Thalassemia: The Think Zinc Study (NCT00459732) | UCSF Benioff Children's Hospital Oakland | 2006-04-01 |
| Invasive Infections in Children With Hemoglobinopathies (NCT00456443) | HaEmek Medical Center, Israel | 2006-01-01 |
| Expanded Access of Deferasirox to Patients With Congenital Disorders of Red Blood Cells and Chronic Iron Overload (NCT00235391) | Novartis Pharmaceuticals | 2005-10-01 |
| Factors Promoting Increased Rate and Success of Pregnancy in the Thalassemia Population in Toronto (NCT00327639) | University Health Network, Toronto | 2005-07-01 |
| Allogeneic Stem Cell Transplantation Following Chemotherapy in Patients With Hemoglobinopathies (NCT00153985) | Dana-Farber Cancer Institute | 2004-03-01 |