Atlas Trials

A Safety and Efficacy Study Evaluating CTX001 in Participants With Transfusion-Dependent β-Thalassemia

Clinical trial NCT03655678 · COMPLETED

Trial details

NCT number
NCT03655678
Sponsor
Vertex Pharmaceuticals Incorporated
Status
COMPLETED
Phase
Phase 2, Phase 3
Study type
INTERVENTIONAL
Beta-ThalassemiaThalassemiaGenetic Diseases, InbornHematologic DiseasesHemoglobinopathies
Start date
2018-09-14
Primary completion
2025-11-13
Enrollment
59

View on ClinicalTrials.gov

Track trials programmatically

Sponsors, conditions and status changes through the Atlas API.