Atlas Trials

Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Transfusion-Dependent β-Thalassemia (TDT)

Clinical trial NCT05356195 · ACTIVE_NOT_RECRUITING

Trial details

NCT number
NCT05356195
Sponsor
Vertex Pharmaceuticals Incorporated
Status
ACTIVE_NOT_RECRUITING
Phase
Phase 3
Study type
INTERVENTIONAL
Beta-ThalassemiaThalassemiaGenetic Diseases, InbornHematologic DiseasesHemoglobinopathies
Start date
2022-05-03
Primary completion
2027-11-14
Enrollment
16

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