Atlas Trials

Translational Potential of ex Vivo Gene Therapy in GM2 Gangliosidosis

Clinical trial NCT07445490 · NOT_YET_RECRUITING

Trial details

NCT number
NCT07445490
Sponsor
Assistance Publique - Hôpitaux de Paris
Status
NOT_YET_RECRUITING
Study type
OBSERVATIONAL
Tay-Sachs Disease GangliosideSandhoff Disease Ganglioside
Start date
2026-05-01
Primary completion
2026-05-01
Enrollment
6

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