Atlas Trials

Sandhoff Disease Ganglioside

2 clinical trials · Condition

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RecordFirmDate
Translational Potential of ex Vivo Gene Therapy in GM2 Gangliosidosis (NCT07445490)Assistance Publique - Hôpitaux de Paris2026-05-01
A Phase I Study of Pyrimethamine in Patients With GM2 Gangliosidosis (NCT00679744)Exsar Corporation2008-05-01

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