Tay-Sachs Disease Ganglioside
2 clinical trials · Condition
◉ Watch Tay-Sachs Disease Ganglioside
| Record | Firm | Date |
|---|---|---|
| Translational Potential of ex Vivo Gene Therapy in GM2 Gangliosidosis (NCT07445490) | Assistance Publique - Hôpitaux de Paris | 2026-05-01 |
| A Phase I Study of Pyrimethamine in Patients With GM2 Gangliosidosis (NCT00679744) | Exsar Corporation | 2008-05-01 |
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