Atlas Trials

A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of Niemann-Pick Type C Disease, GM1 Gangliosidosis or GM2 Gangliosidosis

Clinical trial NCT07054515 · RECRUITING

Trial details

NCT number
NCT07054515
Sponsor
Azafaros B.V.
Status
RECRUITING
Phase
Phase 3
Study type
INTERVENTIONAL
Niemann-Pick Type C DiseaseGM1 GangliosidosisGM2 Gangliosidosis
Start date
2025-06-30
Primary completion
2028-05-14
Enrollment
147

View on ClinicalTrials.gov

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