Pyruvate Carboxylase Deficiency Disease
1 clinical trials · Condition
◉ Watch Pyruvate Carboxylase Deficiency Disease
| Record | Firm | Date |
|---|---|---|
| Compassionate Use of Triheptanoin (C7) for Inherited Disorders of Energy Metabolism (NCT01461304) | Jerry Vockley, MD, PhD |
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