Mucopolysaccharidosis III-A
2 clinical trials · Condition
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| Record | Firm | Date |
|---|---|---|
| Phase I/II Study of JR-441 in Patients With Mucopolysaccharidosis Type IIIA (NCT06095388) | JCR Pharmaceuticals Co., Ltd. | 2023-10-04 |
| A Natural History Study of Biomarkers and Clinical Outcomes in Mucopolysaccharidosis Type IIIA (MPS IIIA; Sanfilippo Syndrome) (NCT05523206) | Sanguine Biosciences | 2022-09-27 |
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