Atlas Trials

Methylmalonic Acidemia

17 clinical trials · Condition

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RecordFirmDate
Long-term Follow-up Study of Patients Who Received hLB-001 Gene Therapy (NCT05506254)Alexion Pharmaceuticals, Inc.2022-07-15
An Observational Study of Carbaglu® for the Treatment of MMA and PA in Adults and Pediatrics (NCT05040178)RECORDATI GROUP2022-06-30
An Extension Study to Evaluate the Long-Term Safety and Clinical Activity of mRNA-3705 in Participants Previously Enrolled in Other Clinical Studies of mRNA-3705 (NCT05295433)ModernaTX, Inc.2022-03-08
Natural History Study of Patients With Methylmalonic Acidemia and Propionic Acidemia (NCT05438485)HemoShear Therapeutics2021-08-27
A Study to Assess the Safety, Pharmacokinetics, and Pharmacodynamics of mRNA-3705 in Participants With Isolated Methylmalonic Acidemia (NCT04899310)ModernaTX, Inc.2021-08-06
Gene Therapy With hLB-001 in Pediatric Patients With Severe Methylmalonic Acidemia (NCT04581785)LogicBio Therapeutics, Inc2021-05-29
A First in Human, Dose Escalation Study to Evaluate the Safety and Tolerability of BBP-671 in Healthy Volunteers and Patients With Propionic Acidemia or Methylmalonic Acidemia (NCT04836494)CoA Therapeutics, Inc., a BridgeBio company2021-03-25
Study of HST5040 in Subjects With Propionic or Methylmalonic Acidemia (NCT04732429)HemoShear Therapeutics2021-03-15
Understanding the Long-Term Management of Organic Acidemia Patients With CARBAGLU®: A Mixed Methods Approach (NCT04176523)RECORDATI GROUP2019-01-15
"The MaP Study": Mapping the Patient Journey in MMA and PA (NCT03484767)ModernaTX, Inc.2018-03-20
Carglumic Acid in Methylmalonic Acidemia and Propionic Acidemia (NCT02426775)King Abdullah International Medical Research Center2015-11-01
Short-Term Outcome of N-Carbamylglutamate in the Treatment of Acute Hyperammonemia (NCT01599286)Mendel Tuchman2012-09-01
Long-term Outcome of N-Carbamylglutamate Treatment in Propionic Acidemia and Methylmalonic Acidemia (NCT01597440)Mendel Tuchman2012-09-01
Combined Malonic and Methylmalonic Aciduria (CMAMMA): Gene Identification and Outcome Study (NCT01289158)McGill University Health Centre/Research Institute of the McGill University Health Centre2011-02-01
Increasing Ureagenesis in Inborn Errors of Metabolism With N-Carbamylglutamate (NCT01341379)Children's Hospital of Philadelphia2010-12-01

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