Atlas Trials

Lysosomal Storage Diseases

20 clinical trials · Condition

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RecordFirmDate
OTL-200 in Patients With Late Juvenile Metachromatic Leukodystrophy (MLD) (NCT04283227)Orchard Therapeutics2022-01-17
Fabry Disease in High-risk Patients With Left Ventricular Hypertrophy: Prevalence and Implementation of a Clinical Score (NCT04943991)Wuerzburg University Hospital2021-07-01
A Pilot Study for Systematic Neonatal Screening for Lysosomal Storage Diseases Using Tandem Mass Spectrometry (NCT04393701)University Hospital, Rouen2021-03-08
A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE) (NCT04093349)Spark Therapeutics, Inc.2020-10-01
Complement Activation in the Lysosomal Storage Disorders (NCT04189601)Melbourne Health2020-09-30
A Long Term Follow-Up Study of Fabry Disease Subjects Treated With FLT190 (NCT04455230)Spur Therapeutics2020-09-08
A Fabry Disease Gene Therapy Study (NCT04040049)Spur Therapeutics2019-07-08
Stem Cell Gene Therapy for Cystinosis (NCT03897361)University of California, San Diego2019-07-08
Neutralizing Antibody Seroprevalence Study With a Retrospective Component in Participants With Late-Onset Pompe Disease (NCT03893240)Spark Therapeutics, Inc.2019-06-12
A Natural History Study of Aspartylglucosaminuria (NCT03853876)Neurogene Inc.2019-04-18
Lyso-Gb1 as a Long-term Prognostic Biomarker in Gaucher Disease (NCT02416661)CENTOGENE GmbH Rostock2018-08-27
Screening of Lysosomal Storage Disorders Diseases in Minority Groups (NCT03812042)Lysosomal and Rare Disorders Research and Treatment Center, Inc.2016-03-17
Natural History Study of Children With Metachromatic Leukodystrophy (NCT01963650)Shire2015-11-02
Longitudinal Study of Neurodegenerative Disorders (NCT03333200)University of Pittsburgh2012-01-11
Fetal Umbilical Cord Blood (UCB) Transplant for Lysosomal Storage Diseases (NCT01003912)Joanne Kurtzberg, MD2009-10-01
Intrathecal Enzyme Replacement Therapy for Spinal Cord Compression in Mucopolysaccharidosis (MPS) I (NCT00215527)Patricia I. Dickson, M.D.2005-11-01

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