Infantile GM2 Gangliosidosis (Disorder)
1 clinical trials · Condition
◉ Watch Infantile GM2 Gangliosidosis (Disorder)
| Record | Firm | Date |
|---|---|---|
| First-in-Human Study of TSHA-101 Gene Therapy for Treatment of Infantile Onset GM2 Gangliosidosis (NCT04798235) | Dr. Anupam Sehgal | 2021-03-12 |
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