Atlas Trials

Gangliosidoses, GM2

3 clinical trials · Condition

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RecordFirmDate
Pyrimethamine as a Treatment for Late-Onset GM2-gangliosidosis (Tay-Sachs and Sandhoff Disease) (NCT01102686)The Hospital for Sick Children2009-08-01
Pharmacokinetics and Tolerability of Zavesca® (Miglustat) In Patients With Juvenile GM2 Gangliosidosis (NCT00418847)The Hospital for Sick Children2004-07-01

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