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Carnitine Palmitoyltransferase Deficiencies (CPT1, CPT2)

1 clinical trials · Condition

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◉ Watch Carnitine Palmitoyltransferase Deficiencies (CPT1, CPT2)

RecordFirmDate
Compassionate Use of Triheptanoin (C7) for Inherited Disorders of Energy Metabolism (NCT01461304)Jerry Vockley, MD, PhD

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Every clearance here is in the API, with alerts when new ones post.