Atlas Trials

Alpha 1 Antitrypsin Deficiency

80 clinical trials · Condition

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RecordFirmDate
Alpha-1 Antitrypsin Disease Cohort: Longitudinal Biomarker Study of Disease (NCT05297812)Columbia University2022-03-23
Functional and Structural Lung Imaging in Chronic Obstructive Pulmonary Disease (NCT04966221)University of Nottingham2022-01-01
An Extension Study of Belcesiran in Patients With Alpha-1 Antitrypsin Deficiency Associated Liver Disease (AATLD) (NCT05146882)Dicerna Pharmaceuticals, Inc., a Novo Nordisk company2021-12-01
A Study of Belcesiran in Patients With AATLD (NCT04764448)Dicerna Pharmaceuticals, Inc., a Novo Nordisk company2021-02-12
Evaluation of the Efficacy and Safety of VX-814 in Subjects With the PiZZ Genotype (NCT04167345)Vertex Pharmaceuticals Incorporated2020-01-13
Phase III, Efficacy and Safety of "Kamada-AAT for Inhalation" (NCT04204252)Kamada, Ltd.2019-11-25
Study of DCR-A1AT in Healthy Adult Volunteers (NCT04174118)Dicerna Pharmaceuticals, Inc., a Novo Nordisk company2019-10-24
Respreeza® Self-administration and Learning Program (AmAREtTI Study) (NCT04262284)CSL Behring2019-10-18
Safety, Tolerability and Pharmacodynamic Effect of Fazirsiran (TAK-999, ARO-AAT) (NCT03945292)Arrowhead Pharmaceuticals2019-08-07
Phase 1 Study to Assess the Safety, PK and PD of INBRX-101 in Adults With Alpha-1 Antitrypsin Deficiency (NCT03815396)Inhibrx Biosciences, Inc2019-07-19
Alpha-1 Research Registry (NCT04157049)Alpha-1 Foundation2019-06-20
Effects of Different Exercise Training Modalities in Alpha-1 Antitrypsin Deficiency Patients (NCT03802357)Schön Klinik Berchtesgadener Land2019-01-10
Long-Term Follow-up Study of ADVM-043 (NCT03804021)Adverum Biotechnologies, Inc.2018-12-27
A 12-week Study Treating Participants Who Have alpha1-antitrypsin-related COPD With Alvelestat (MPH966) or Placebo. (NCT03636347)Mereo BioPharma2018-10-29
Study Comparing Weekly Intravenous Administration of OctaAlpha1 With a Marketed Preparation Glassia® in Subjects With Alpha-1-antitrypsin Deficiency (NCT03385395)Octapharma2018-07-01
Exploring the Utility of Hyperpolarized 129Xe MRI in Healthy Volunteers and Patients With Lung Disease (NCT03455686)McMaster University2018-04-19
Study of ARO-AAT in Normal Adult Volunteers (NCT03362242)Arrowhead Pharmaceuticals2018-03-12
Czech AATD Registry (NCT05178277)Thomayer University Hospital2018-01-01
Safety Dose Finding Study of ADVM-043 Gene Therapy to Treat Alpha-1 Antitrypsin (A1AT) Deficiency (NCT02168686)Adverum Biotechnologies, Inc.2017-11-28
The Effects of Discontinuation of Vitamin K Antagonists on the Rate of Elastin Degradation (NCT03285100)Canisius-Wilhelmina Hospital2017-10-31
Efficacy/Safety of HA Inhalation Solution for Hereditary Emphysema in Patients With Alpha-1 Antitrypsin Deficiency (NCT03114020)Gerard Turino2017-03-22
Targeting Pulmonary Perfusion in Alpha-1 Antitrypsin Deficiency (NCT03008915)Columbia University2017-01-01
The Impact of Delayed Diagnosis of Alpha-1 Antitrypsin Deficiency (NCT03039335)Biocerna LLC2016-12-15
Safety, Tolerability and Effect of ARC-AAT Injection on Circulating and Intrahepatic Alpha-1 Antitrypsin Levels (NCT02900183)Arrowhead Pharmaceuticals2016-10-01
Epigenetic Regulation of Immunity in Alpha-1 Anti-trypsin Deficiency (NCT02691611)National Jewish Health2015-12-01
Environment Effect on Six-Minute Walk Test Performance (NCT02502201)University of Florida2015-10-01
Microbioma in Sputa From COPD With Alpha-1 Antitrypsin Deficiency (NCT02547532)Fondazione Salvatore Maugeri2015-09-01
A Study of ARC-AAT in Healthy Volunteer Subjects and Patients With Alpha-1 Antitrypsin Deficiency (AATD) (NCT02363946)Arrowhead Pharmaceuticals2015-02-01
Alpha-1 Carrier Genomics Study (NCT02810327)Medical University of South Carolina2015-02-01
Lung Volume Reduction Coils for Emphysema in Alpha-1 Antitrypsin Deficiency (NCT02273349)University Hospital, Saarland2014-10-01
Phase II, Safety and Efficacy Study of Kamada-alpha-1-antitrypsin (AAT) for Inhalation" (NCT02001688)Kamada, Ltd.2014-04-01
Alpha-1 Antitrypsin Deficiency Adult Liver Study (NCT02014415)St. Louis University2013-12-01
Ex-vivo Perfusion and Ventilation of Lungs Recovered From Non-Heart-Beating Donors to Assess Transplant Suitability (NCT01615484)University of North Carolina, Chapel Hill2013-09-01
Genomic Research in Alpha-1 Antitrypsin Deficiency (NCT01832220)University of Pittsburgh2013-05-01
Effect of Double Dose of Alpha 1-antitrypsin Augmentation Therapy on Lung Inflammation. (NCT01669421)Michael Campos, MD2012-07-01
Carbamazepine in Severe Liver Disease Due to Alpha-1 Antitrypsin Deficiency (NCT01379469)Washington University School of Medicine2012-01-01
Phase 2 Study of Ex-vivo Perfusion and Ventilation of Lungs to Assess Transplant Suitability (NCT01241942)University of North Carolina, Chapel Hill2010-12-01
Safety & Efficacy Study of rAAV1-CB-hAAT for Alpha-1 Antitrypsin Deficiency (NCT01054339)Beacon Therapeutics2010-06-01
Effects of Exercise Training in Chronic Obstructive Pulmonary Disease Versus Alpha-1-Antitrypsin-deficiency-patients (NCT01380626)Schön Klinik Berchtesgadener Land2010-02-01
Prevalence of Alpha-1 Antitrypsin Deficiency in Chronic Obstructive Pulmonary Disease (COPD) (NCT01419158)Alpha-1 Foundation2008-01-01
Longitudinal Study of Genetic Causes of Intrahepatic Cholestasis (LOGIC) (NCT00571272)Arbor Research Collaborative for Health2007-11-30
Lung Disease and Its Affect on the Work of White Blood Cells in the Lungs (NCT01851642)University of Florida2007-08-09
The Use of High Resolution Chest Computed Tomography in Alpha-1 Antitrypsin Deficiency (NCT00532805)Medical University of South Carolina2007-08-01
Phase II/III Study of an Alpha-1 Proteinase Inhibitor (Kamada-API) in Individuals With Alpha-1 Antitrypsin Deficiency (NCT00460096)Kamada, Ltd.2007-03-01
Efficacy and Safety Study of Augmentation Therapy With ARALAST Fraction IV-1 (Human Alpha 1 - Proteinase Inhibitor) (NCT00396006)Baxalta now part of Shire2006-10-27
The Safety and Tolerability of Alpha-1 Modified Process (MP) In Subjects With Alpha-1-antitrypsin (AAT) Deficiency (NCT00301366)Grifols Therapeutics LLC2006-06-01
Comparison of Pharmacokinetic, Safety, Tolerability of Alpha-1 MP and Prolastin In Alpha1-antitrypsin Deficient Adults (NCT00295061)Grifols Therapeutics LLC2006-05-01
Experimental Gene Transfer Procedure to Treat Alpha 1-Antitrypsin (AAT) Deficiency (NCT00430768)University of Massachusetts, Worcester2006-02-01
Pharmacokinetic Study of ARALAST (Human Alpha1- PI) (NCT00242385)Baxalta now part of Shire2005-12-20
Management of Patients With Alpha-1 Antitrypsin Deficiency Associated Emphysema (NCT00700934)Assistance Publique - Hôpitaux de Paris2005-02-01
Experimental Gene Transfer Procedure to Treat Alpha 1-Antitrypsin Deficiency (NCT00377416)University of Massachusetts, Worcester2004-03-01
Alpha-1-Antitrypsin (AAT) To Treat Emphysema In AAT-Deficient Patients (EXACTLE) (NCT00263887)Grifols Therapeutics LLC2003-12-01
Alpha-1 Foundation DNA and Tissue Bank (NCT00884455)University of Florida2002-12-01
4-PBA: Will it Increase the Level of Alpha 1-Antitrypsin(AAT) in Persons With AAT Deficiency? (NCT00067756)University of Florida2001-11-01
Alpha-1 Foundation Research Registry (NCT00499941)Medical University of South Carolina2000-04-01
Study of Genotype and Phenotype in Patients With Alpha 1-Antitrypsin Deficiency (NCT00005098)National Center for Research Resources (NCRR)1999-03-01
Characterization of the Pathobiology of Early Lung Destruction in Alpha 1-Antitrypsin Deficient Individuals (NCT00001462)National Heart, Lung, and Blood Institute (NHLBI)1995-05-01
Alpha1-antitrypsin Deficiency Registry (NCT00005292)National Heart, Lung, and Blood Institute (NHLBI)1988-09-01
Early Access Program Using Alpha 1 Antitrypsin Infusion for Patients With Steroid Refractory Acute GvHD After Hematopoietic Stem Cell Transplantation (HSCT) (NCT03172455)Impatients N.V. trading as myTomorrows

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