Atlas Trials

Achondroplasia

46 clinical trials · Condition

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RecordFirmDate
Adaption and Testing of the Quality of Life in Short Stature Youth (QoLISSY) Questionnaire for Parents With Children From 0-4 (NCT05603936)Universitätsklinikum Hamburg-Eppendorf2022-03-01
A Dose Escalation Trial Evaluating Safety, Efficacy, and Pharmacokinetics of Multiple Subcutaneous Doses of TransCon CNP Administered Once Weekly in Children With Achondroplasia (NCT05246033)Visen Pharmaceuticals (Shanghai) Co., Ltd.2022-01-05
Continuation Study of Long-term Safety, Tolerability, Pharmacokinetics and Efficacy of Recifercept in Achondroplasia (NCT05116046)Pfizer2021-12-24
Extension Study of Infigratinib in Children With Achondroplasia (ACH) (NCT05145010)QED Therapeutics, a BridgeBio company2021-12-06
Registry for Patients With Achondroplasia / Hypochondroplasia (OMPR-Ach/Hy) (NCT05328050)Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico2021-09-01
A Study Of Safety, Tolerability And Effectiveness Of Recifercept In Children With Achondroplasia (NCT04638153)Pfizer2020-12-02
A Clinical Trial to Evaluate Safety of Vosoritide in At-risk Infants With Achondroplasia (NCT04554940)BioMarin Pharmaceutical2020-10-10
A Dose Escalation Trial Evaluating Safety, Efficacy, and Pharmacokinetics of TransCon CNP Administered Once Weekly in Prepubertal Children With Achondroplasia (NCT04085523)Ascendis Pharma A/S2020-06-24
Study of Infigratinib in Children With Achondroplasia (NCT04265651)QED Therapeutics, a BridgeBio company2020-03-10
Radiological Analysis on Patients With Achondroplasia Disorder (NCT04184817)Hospices Civils de Lyon2020-02-15
Prospective Clinical Assessment Study in Children With Achondroplasia (ACH) (NCT04035811)QED Therapeutics, a BridgeBio company2019-08-12
A Multi-center, Longitudinal, Observational Study of Children With Achondroplasia (NCT03875534)Ascendis Pharma A/S2019-06-19
An Extension Study to Evaluate Safety and Efficacy of BMN 111 in Children With Achondroplasia (NCT03989947)BioMarin Pharmaceutical2019-06-12
Lifetime Impact Study for Achondroplasia (NCT03872531)BioMarin Pharmaceutical2019-03-31
Observational Study Investigating Clinical & Anthropometric Characteristics of Children With Achondroplasia. (NCT03794609)Pfizer2018-06-15
A Clinical Trial to Evaluate the Safety and Efficacy of BMN 111 in Infants and Young Children With Achondroplasia (NCT03583697)BioMarin Pharmaceutical2018-06-13
Lifetime Impact of Achondroplasia Study in Europe-LIAISE (NCT03449368)BioMarin Pharmaceutical2017-12-17
An Extension Study to Evaluate the Efficacy and Safety of BMN 111 in Children With Achondroplasia (NCT03424018)BioMarin Pharmaceutical2017-12-12
The Norwegian Adult Achondroplasia Study (NCT03780153)Sunnaas Rehabilitation Hospital2017-03-01
A Study to Evaluate the Efficacy and Safety of BMN 111 in Children With Achondroplasia (NCT03197766)BioMarin Pharmaceutical2016-12-12
Achondroplasia Natural History Multicenter Clinical Study (NCT02597881)Johns Hopkins University2016-04-01
A Study to Evaluate Long-Term Safety, Tolerability, & Efficacy of BMN 111 in Children With Achondroplasia (ACH) (NCT02724228)BioMarin Pharmaceutical2016-01-26
A Phase 2 Study of BMN 111 to Evaluate Safety, Tolerability, and Efficacy in Children With Achondroplasia (NCT02055157)BioMarin Pharmaceutical2014-01-13
A Survey Collecting Data on Adult Height in Patients With Achondroplasia Treated With Somatropin (NCT01435629)Novo Nordisk A/S2012-11-22
A Multicenter, Multinational Clinical Assessment Study for Pediatric Patients With Achondroplasia (NCT01603095)BioMarin Pharmaceutical2012-04-01
A Study to Evaluate Safety and Tolerability of BMN 111 Administered to Healthy Adult Volunteers (NCT01590446)BioMarin Pharmaceutical2012-02-01
C-Type Natriuretic Peptide and Achondroplasia (NCT01541306)Nemours Children's Clinic2012-02-01
Special Survey for Long Term Application (NCT01516229)Novo Nordisk A/S1997-05-01
Issues Surrounding Prenatal Genetic Testing for Achondroplasia (NCT00001536)National Human Genome Research Institute (NHGRI)1996-08-01

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