Study of the Safety and Efficacy of an Adeno-Associated Viral Vector Carrying the SMN Gene After a Single Intravenous Administration of Escalating Doses in Children With Spinal Muscular Atrophy (BLUEBELL)
Clinical trial NCT05747261 · RECRUITING
Trial details
- NCT number
- NCT05747261
- Sponsor
- Biocad
- Status
- RECRUITING
- Phase
- Phase 1, Phase 2
- Study type
- INTERVENTIONAL
- Start date
- 2023-02-02
- Primary completion
- 2025-09-01
- Enrollment
- 40
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