Study of Ataluren (PTC124) in Nonambulatory Participants With Nonsense-Mutation-Mediated Duchenne/Becker Muscular Dystrophy (nmDMD/BMD)
Clinical trial NCT01009294 · TERMINATED
Trial details
- NCT number
- NCT01009294
- Sponsor
- PTC Therapeutics
- Status
- TERMINATED
- Phase
- Phase 2
- Study type
- INTERVENTIONAL
- Start date
- 2010-01-13
- Primary completion
- 2010-03-23
- Enrollment
- 6
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