Atlas Trials

Safety and Efficacy of AAV9/AP4B1 (BFB-101) For Patients With AP4B1-related Hereditary Spastic Paraplegia Type 47 (SPG47)

Clinical trial NCT06948019 · NOT_YET_RECRUITING

Trial details

NCT number
NCT06948019
Sponsor
BlackfinBio Ltd
Status
NOT_YET_RECRUITING
Phase
Phase 1, Phase 2
Study type
INTERVENTIONAL
HSPHereditary Spastic ParaplegiaHereditary Spastic ParaparesisHereditary Spastic Paraplegia Type 50Hereditary Spastic Paraplegia Type 47Hereditary Spastic Paraplegia Type 51Hereditary Spastic Paraplegia Type 52SPG47AP4B1Neurogenetic DisordersNeurodevelopmental ConditionsMovement Disorders
Start date
2025-08-01
Primary completion
2030-08-01
Enrollment
5

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