Phase I/II/III Gene Transfer Clinical Trial of scAAV9.U1a.hSGSH

Clinical trial NCT02716246 · RECRUITING

Trial details

NCT number: NCT02716246
Sponsor: Ultragenyx Pharmaceutical Inc
Status: RECRUITING
Phase: Phase 2, Phase 3
Study type: INTERVENTIONAL

MPS IIIA Sanfilippo Syndrome Sanfilippo A Mucopolysaccharidosis III

Start date: 2016-04-25
Primary completion: 2029-03-01
Enrollment: 36

View on ClinicalTrials.gov

Track trials programmatically

Sponsors, conditions and status changes through the Atlas API.