PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)

Clinical trial NCT04532047 · RECRUITING

Trial details

NCT number: NCT04532047
Sponsor: University of California, San Francisco
Status: RECRUITING
Phase: Phase 1
Study type: INTERVENTIONAL

MPS I MPS II MPS IVA MPS VI Mps VII Gaucher Disease, Type 2 Gaucher Disease, Type 3 Pompe Disease Infantile-Onset Wolman Disease

Start date: 2021-07-01
Primary completion: 2031-07-31
Enrollment: 10

View on ClinicalTrials.gov

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