Atlas Trials

Long-Chain Fatty Acid Oxidation Disorders (LC-FAOD) Extension Study for Subjects Previously Enrolled in Triheptanoin Studies

Clinical trial NCT02214160 · COMPLETED

Trial details

NCT number
NCT02214160
Sponsor
Ultragenyx Pharmaceutical Inc
Status
COMPLETED
Phase
Phase 2
Study type
INTERVENTIONAL
Carnitine Palmitoyltransferase (CPT I or CPT II) DeficiencyVery Long Chain Acyl-CoA Dehydrogenase (VLCAD) DeficiencyLong-chain 3-hydroxy-acyl-CoA Dehydrogenase (LCHAD) DeficiencyTrifunctional Protein (TFP) DeficiencyCarnitine-acylcarnitine Translocase (CACT) Deficiency
Start date
2014-12-09
Primary completion
2020-12-03
Enrollment
94

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