Atlas Trials

Hematopoietic Stem Cell Transplantation (HSCT) for Common Variable Immunodeficiency (CVID) and Other Autoimmune Manifestations of Primary Immune Regulatory Disorders (PIRD)

Clinical trial NCT07284641 · RECRUITING

Trial details

NCT number
NCT07284641
Sponsor
Paul Szabolcs
Status
RECRUITING
Phase
Phase 2
Study type
INTERVENTIONAL
Common Variable Immunodeficiency (CVID)Primary Immune Regulatory DisorderImmune DysregulationDiGeorge SyndromeSTAT 1 Gain of FunctionSTAT 3 Gain of FunctionHypomorphic RAG1 DeficiencyCD40 Ligand DeficiencyMendelian Susceptibility to Mycobacterial DiseaseGATA2 Associated ImmunodeficiencyCD40 DeficiencyHypomorphic RAG2 Deficiency
Start date
2026-05-04
Primary completion
2030-05-04
Enrollment
25

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