GNE-Myopathy Disease Monitoring Program (GNEM-DMP): A Registry and Prospective Observational Natural History Study to Assess GNE Myopathy or Hereditary Inclusion Body Myopathy (HIBM)

Clinical trial NCT01784679 · COMPLETED

Trial details

NCT number: NCT01784679
Sponsor: Ultragenyx Pharmaceutical Inc
Status: COMPLETED
Study type: OBSERVATIONAL

Hereditary Inclusion Body Myopathy GNE Myopathy Nonaka Disease Quadriceps Sparing Myopathy (QSM)Distal Myopathy With Rimmed Vacuoles (DMRV)

Start date: 2013-04-05
Primary completion: 2017-11-30
Enrollment: 319

View on ClinicalTrials.gov

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