Atlas Trials

Gene Transfer Study of ABO-102 in Patients With Middle and Advanced Phases of MPS IIIA Disease

Clinical trial NCT04088734 · TERMINATED

Trial details

NCT number
NCT04088734
Sponsor
Ultragenyx Pharmaceutical Inc
Status
TERMINATED
Phase
Phase 1, Phase 2
Study type
INTERVENTIONAL
MPS IIIASanfilippo SyndromeSanfilippo AMucopolysaccharidosis III
Start date
2019-09-18
Primary completion
2022-03-10
Enrollment
5

View on ClinicalTrials.gov

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