Atlas Trials

EPI-743 in Cobalamin C Defect: Effects on Visual and Neurological Impairment

Clinical trial NCT01793090 · COMPLETED

Trial details

NCT number
NCT01793090
Sponsor
Bambino Gesù Hospital and Research Institute
Status
COMPLETED
Phase
Phase 2
Study type
INTERVENTIONAL
Methylmalonic Aciduria and Homocystinuria,Cblc TypeGenetic DiseaseRetinopathy
Start date
2013-01-01
Primary completion
2013-07-01
Enrollment
30

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