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Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)

Clinical trial NCT07608432 · RECRUITING

Trial details

NCT number
NCT07608432
Sponsor
Dyne Therapeutics
Status
RECRUITING
Phase
Phase 3
Study type
INTERVENTIONAL
Duchenne Muscular Dystrophy (DMD)Muscular Dystrophy, DuchenneMuscular Dystrophy (DMD)DMDMuscular DystrophiesMuscular Dystrophy in ChildrenMuscular Dystrophy, Duchenne TypeMuscular Dystrophy, Duchenne and Becker TypesMuscular Dystrophies (Duchenne, Becker, Myotonic Dystrophy)Genetic Disease, InbornGenetic Disease, X-LinkedCongenital, Hereditary, and Neonatal Diseases and Abnormalities
Start date
2026-06-01
Primary completion
2030-12-01
Enrollment
90

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