An Open-Label Phase 1/2 Study to Assess the Safety, Efficacy and Dose of Study Drug UX003 Recombinant Human Beta-glucuronidase (rhGUS) Enzyme Replacement Therapy in Patients With Mucopolysaccharidosis Type 7 (MPS 7)
Clinical trial NCT01856218 · COMPLETED
Trial details
- NCT number
- NCT01856218
- Sponsor
- Ultragenyx Pharmaceutical Inc
- Status
- COMPLETED
- Phase
- Phase 1, Phase 2
- Study type
- INTERVENTIONAL
- Start date
- 2013-11-01
- Primary completion
- 2016-07-01
- Enrollment
- 3
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