A Study to Evaluate the Efficacy and Safety of Mitapivat in Pediatric Participants With Pyruvate Kinase Deficiency (PKD) Who Are Regularly Transfused, Followed by a 5-Year Extension Period

Clinical trial NCT05144256 · ACTIVE_NOT_RECRUITING

Trial details

NCT number: NCT05144256
Sponsor: Agios Pharmaceuticals, Inc.
Status: ACTIVE_NOT_RECRUITING
Phase: Phase 3
Study type: INTERVENTIONAL

Pediatric Pyruvate Kinase Deficiency Pediatric Hemolytic Anemia

Start date: 2022-06-08
Primary completion: 2024-05-03
Enrollment: 49

View on ClinicalTrials.gov

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