Atlas Trials

A Study to Evaluate Efficacy, Safety, Tolerability and Exposure After a Repeat-dose of Sepofarsen (QR-110) in LCA10 (ILLUMINATE)

Clinical trial NCT03913143 · ACTIVE_NOT_RECRUITING

Trial details

NCT number
NCT03913143
Sponsor
ProQR Therapeutics
Status
ACTIVE_NOT_RECRUITING
Phase
Phase 2, Phase 3
Study type
INTERVENTIONAL
Leber Congenital Amaurosis 10BlindnessLeber Congenital AmaurosisVision DisordersSensation DisordersNeurologic ManifestationsEye DiseasesEye Diseases, HereditaryEye Disorders CongenitalRetinal Disease
Start date
2019-04-04
Primary completion
2022-01-31
Enrollment
36

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