A Study to Assess the Safety, Tolerability, and Efficacy of Long-term SOBI003 Treatment in Pediatric MPS IIIA Patients

Clinical trial NCT03811028 · COMPLETED

Trial details

NCT number: NCT03811028
Sponsor: Swedish Orphan Biovitrum
Status: COMPLETED
Phase: Phase 1, Phase 2
Study type: INTERVENTIONAL

Sanfilippo Syndrome Type A (MPS IIIA)

Start date: 2019-01-19
Primary completion: 2021-04-30
Enrollment: 6

View on ClinicalTrials.gov

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