Atlas Trials

A Real-world Long-term Safety and Immunogenicity Study of Olipudase Alfa Therapy in Pediatric Patients Less Than 2 Years of Age With Acid Sphingomyelinase Deficiency (ASMD)

Clinical trial NCT06192576 · RECRUITING

Trial details

NCT number
NCT06192576
Sponsor
Sanofi
Status
RECRUITING
Study type
OBSERVATIONAL
Niemann-Pick DiseasesAcid Sphingomyelinase Deficiency
Start date
2024-04-16
Primary completion
2029-01-02
Enrollment
10

View on ClinicalTrials.gov

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