A Phase 1/2 Study of Intravenous Gene Transfer With an AAV9 Vector Expressing Human Beta-galactosidase in Type I and Type II GM1 Gangliosidosis
Clinical trial NCT03952637 · RECRUITING
Trial details
- NCT number
- NCT03952637
- Sponsor
- National Human Genome Research Institute (NHGRI)
- Status
- RECRUITING
- Phase
- Phase 1, Phase 2
- Study type
- INTERVENTIONAL
- Start date
- 2019-08-19
- Primary completion
- 2028-01-01
- Enrollment
- 54
Track trials programmatically
Sponsors, conditions and status changes through the Atlas API.