Atlas Trials

A Dose-escalation and Safety & Efficacy Study of AXO-AAV-GM2 in Tay-Sachs or Sandhoff Disease

Clinical trial NCT04669535 · TERMINATED

Trial details

NCT number
NCT04669535
Sponsor
Terence Flotte
Status
TERMINATED
Phase
Phase 1
Study type
INTERVENTIONAL
Tay-Sachs DiseaseSandhoff Disease
Start date
2021-01-15
Primary completion
2024-05-23
Enrollment
9

View on ClinicalTrials.gov

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